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F783L

Category 4 — Stable Fold, Function DisruptedConflictingLumenal · predictedσ-1 candidateEditorial
PhenylalanineLeucine at position 783 · C-terminal lumenal domain (653-869) · WFS1 (Wolframin)

Phenylalanine → Leucine at position 783 in lumenal domain. ClinVar Conflicting including WFS1 spectrum. AlphaMissense 0.414 (below threshold), ΔΔG -0.22. pLDDT 61 borderline.

Interactive 3D Structure

Wild-type reference
Wild-type F783 — hydrogen bond to S785
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DynaMut2 mutant · F783L
Mutant L783 — polar contact contact to M781 lost
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Bond changes · DynaMut2 interaction analysis

0 lost2 gained4 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondM781Gained
Hydrogen bondS785S785Preserved
Polar contactM781M781Preserved
Polar contactS785S785Preserved
HydrophobicQ667Q667Preserved
HydrophobicK800Gained

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-0.22kcal/mol
Destabilising — mild
AlphaMissense
0.414
Amb
AlphaFold pLDDT
61
model confidence
Schema
Cat 4
Category 4 — Stable Fold, Function Disrupted

Clinical Evidence

ClinVar classificationConflicting classifications of pathogenicity
Review statuscriteria provided, conflicting classifications
Associated conditionsWFS1-Related Spectrum Disorders; Inborn genetic diseases
InheritanceWFS1 spectrum.
Population frequency (gnomAD v4)Ultra-rare · AF 0.0069%
cDNA changec.2347T>C
ClinVar accessionVCV000215370
Last evaluated2025/07/31 00:00

Observed at very low frequency in gnomAD.

Structural Context

Position 783 in lumenal domain. Neighbors: PRO782 (2.5 Å — partner of G702S neighbor P782), SER784 (2.5 Å), GLN667 (4.4 Å — long-range to Y669 cluster), SER785 (4.7 Å).

F783L removes aromatic. Q667 long-range contact suggests F783 mediates packing between this site and the Y669-C673 cluster. AM 0.414 under-call; WFS1 spectrum confirms pathogenicity.

Amino-acid chemistry
Phenylalanine (F) → Leucine (L) — aromatic replaced by branched aliphatic. Aromatic loss.
Position in the protein
C-terminal lumenal domain · position 783 (pLDDT 61 borderline).

Druggability Assessment

Category 4 — Stable Fold, Function Disrupted (AM under-call, pLDDT borderline). |ΔΔG| 0.22. AlphaMissense 0.414 below threshold.

Mechanism: lost aromatic + perturbation of long-range Q667 contact. Therapeutic: 783-667 cross-domain.

Why this matters

F783L identifies a long-range contact to the Y669-Q667 cluster.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the F783L PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download F783L PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Topological domain653869 · Lumenal