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L672P

Category 3/4 — Most DruggableLikely pathogenicLumenal · predictedσ-1 candidateEditorial
LeucineProline at position 672 · C-terminal lumenal domain (653-869) · WFS1 (Wolframin)

Leucine → Proline at position 672 in wolframin's C-terminal lumenal domain. ClinVar Likely pathogenic. AlphaMissense 0.947, DynaMut2 ΔΔG -0.28 kcal/mol (destabilising). A proline-introduction variant adjacent to C673 (the cysteine partner in the C690R disulfide discussion).

Interactive 3D Structure

Wild-type reference
Wild-type L672 — hydrogen bond to Q668
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DynaMut2 mutant · L672P
Mutant P672 — hydrogen bond to Q668 lost (4 contacts lost)
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Bond changes · DynaMut2 interaction analysis

4 lost0 gained4 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondQ668Q668Preserved
Hydrogen bondY669Lost
Polar contactQ668Q668Preserved
Polar contactY669Lost
Polar contactA677A677Preserved
Polar contactT686T686Preserved
HydrophobicL689Lost
HydrophobicL693Lost

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-0.28kcal/mol
Destabilising — mild
AlphaMissense
0.947
LPath
AlphaFold pLDDT
88
model confidence
Schema
Cat 3/4
Category 3/4 — Most Druggable
ΔΔG confidence: Standard confidence · Lumenal

This variant is in a water-facing region, which is the regime the stability predictor was built and benchmarked for. Ordinary predictor error still applies.

Clinical Evidence

ClinVar classificationLikely pathogenic
Review statuscriteria provided, single submitter
Associated conditions(no specific conditions catalogued)
InheritanceInheritance not specified.
Population frequency (gnomAD v4)Ultra-rare · AF 0.00048%
cDNA changec.2015T>C
ClinVar accessionVCV000918069
Last evaluated2025/07/24 00:00

Observed at very low frequency in gnomAD.

Classified for1★ unverified submission

ClinVar classifies this variant as Likely pathogenic, but does not state what it is classified for. ClinVar records the condition only as "not provided". A classification without a phenotype and an inheritance mode cannot be read as a statement about Wolfram syndrome risk or severity.

  • Phenotype scope is interpretation of submitted records. The computed values on this card (AlphaMissense, DynaMut2 ΔΔG, pLDDT) are measurements of the model, not of a patient.
  • Presentation cannot be generalised from neighbouring variants: one nucleotide over can present very differently. Structural similarity supports a mechanistic hypothesis, never a phenotype claim.

Review status: 1★ single submitter. ClinVar "conditions" is the union of all submissions; 0–1★ entries are submitted conditions, not documented phenotypes.

Population frequency
Global (all ancestries)
AF 0.00048% · 7 / 1,460,984 alleles
Homozygotes
0
Highest-frequency population
Remaining individuals · AF 0.0050%

Highest in Remaining individuals: AF 0.0050% (3 of 60,382 alleles), 10.4x the global figure. The global AF describes the general population, not the at-risk group.

No homozygotes reported in gnomAD v4. For a recessive allele this is expected and is not, on its own, evidence either way.

Ancestry groupAllele freq.AC / ANHom.Carrier est.
Remaining individuals0.0050%3 / 60,3820~1 in 10060
European (non-Finnish)0.00036%4 / 1,112,0040~1 in 139000

Source: gnomAD r4, retrieved 2026-08-21. Values are allele frequencies. The carrier estimate is derived from the allele frequency (Hardy-Weinberg, ~2·AF) and is an approximation, not a published figure — where a published carrier frequency exists it outranks this column and is cited on the card.

Structural Context

Position 672 sits in wolframin's C-terminal lumenal domain. The AlphaFold model places L672 within 5 Å of CYS673 (2.4 Å — same C673 discussed in C690R/C690Y Atlas cards for the inferred disulfide), ALA671 (2.5 Å), TYR669 (3.8 Å — partner of Y669C/Y669H), GLN668 (4.1 Å), and ALA677 (4.5 Å).

The wild-type leucine at 672 contributes hydrophobic packing in a region densely populated by structurally important residues: C673 (potential disulfide), Y669 (aromatic packing partner), Q668. Replacing it with proline introduces a backbone kink that perturbs the geometry of this multi-residue contact cluster.

The |ΔΔG| of 0.28 reflects fold accommodation. AlphaMissense's 0.947 confirms severe functional consequence. The mechanism is geometric — backbone kink propagates through the C673-Y669-Q668 microregion.

Amino-acid chemistry
Leucine (L) → Proline (P) — flexible branched hydrophobic replaced by rigid helix-breaking residue.
Position in the protein
C-terminal lumenal domain · position 672 in the ER lumen (pLDDT 88).

Druggability Assessment

Category 3/4 — Most Druggable. |ΔΔG| = 0.28 — fold survives. AlphaMissense 0.947 confirms severe functional consequence.

Mechanism is proline-induced backbone kink near the C673-Y669 microregion (shared with Y669C, Y669H, C690R, C690Y atlas cards). Therapeutic strategy: site-directed at this dense contact cluster.

Why this matters

L672P sits adjacent to the C673-Y669-C690 cluster — one of the densest variant-target hubs in the Atlas. Multiple variants converge here, all with site-directed rescue opportunities.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the L672P PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download L672P PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Topological domain653869 · Lumenal