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L842F

Category 3/4 — Most DruggableLikely pathogenicLumenal · predictedσ-1 candidateEditorial
LeucinePhenylalanine at position 842 · C-terminal lumenal domain (653-869) · WFS1 (Wolframin)

Leucine → Phenylalanine at position 842 in wolframin's C-terminal lumenal domain. ClinVar Likely pathogenic. AlphaMissense 0.956, DynaMut2 ΔΔG -0.61 kcal/mol (destabilising). Volume increase variant near the L829 region.

Interactive 3D Structure

Wild-type reference
Wild-type L842 — hydrogen bond to R805
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DynaMut2 mutant · L842F
Mutant F842 — polar contact contact to R805 lost
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Bond changes · DynaMut2 interaction analysis

1 lost5 gained10 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondR805R805Preserved
Hydrogen bondS826Gained
Hydrogen bondA844Gained
Polar contactR805R805Preserved
Polar contactF810F810Preserved
Polar contactA844A844Preserved
Aromatic / πF810Gained
Van der WaalsF810F810Preserved
Van der WaalsA844Gained
HydrophobicI777I777Preserved
HydrophobicL804L804Preserved
HydrophobicA806A806Preserved
HydrophobicF810F810Preserved
HydrophobicL814Gained
HydrophobicF825Lost
HydrophobicI845I845Preserved

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-0.61kcal/mol
Destabilising — mild
AlphaMissense
0.956
LPath
AlphaFold pLDDT
89
model confidence
Schema
Cat 3/4
Category 3/4 — Most Druggable

Clinical Evidence

ClinVar classificationLikely pathogenic
Review statuscriteria provided, single submitter
Associated conditions(no specific conditions catalogued)
InheritanceInheritance not specified.
Population frequency (gnomAD v4)Ultra-rare · AF 0.00019%
cDNA changec.2524C>T
ClinVar accessionVCV001518006
Last evaluated2023/03/23 00:00

Observed at very low frequency in gnomAD.

Structural Context

Position 842 sits in wolframin's C-terminal lumenal domain. The AlphaFold model places L842 within 5 Å of GLU841 (2.5 Å), LYS843 (2.5 Å — same K843 as the K862-K843 cluster), ARG805 (3.7 Å — long-range, near A806P), SER826 (4.2 Å), and ALA844 (4.7 Å).

The wild-type leucine fits cleanly into this mixed polar-basic environment. Replacing it with phenylalanine adds aromatic volume that the local pocket was not sized for. The K843 + L842 + R805 region is reorganized.

The |ΔΔG| of 0.61 reflects modest fold cost. AlphaMissense's 0.956 confirms severe functional consequence. The proximity to A806P (3.7 Å through R805) and the K843 contact suggest this region is a multi-variant hub.

Amino-acid chemistry
Leucine (L) → Phenylalanine (F) — branched aliphatic hydrophobic replaced by aromatic hydrophobic. Volume increase, aromatic π-system added.
Position in the protein
C-terminal lumenal domain · position 842 in the ER lumen (pLDDT 89).

Druggability Assessment

Category 3/4 — Most Druggable. |ΔΔG| = 0.61 — fold survives. AlphaMissense 0.956 confirms severe functional consequence.

Mechanism is volume mismatch in the E841-L842-K843-R805 polar-basic environment. Therapeutic strategy: site-directed at this microregion.

Why this matters

L842F joins A806P and the K843/K862 cluster as part of a multi-variant lumenal C-terminal target region.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the L842F PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download L842F PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Topological domain653869 · Lumenal