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R517C

Category 4 — Stable Fold, Function DisruptedConflictingTransmembrane · predictedEditorial
ArginineCysteine at position 517 · Connecting loop · WFS1 (Wolframin)

Arginine → Cysteine at position 517 in connecting loop. ClinVar Conflicting including Wolfram-like + Cataract 41. AlphaMissense 0.16 (below threshold) — AM under-call. DynaMut2 ΔΔG -0.89. Same loop region as M518I, M518K.

Interactive 3D Structure

Wild-type reference
Wild-type R517 — hydrogen bond to L521
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DynaMut2 mutant · R517C
Mutant C517 — hydrogen bond contact to Y513 lost
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Bond changes · DynaMut2 interaction analysis

1 lost1 gained12 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondY513Y513Preserved
Hydrogen bondL514L514Preserved
Hydrogen bondQ520Q520Preserved
Hydrogen bondL521L521Preserved
Polar contactY513Y513Preserved
Polar contactL514L514Preserved
Polar contactF515F515Preserved
Polar contactQ520Q520Preserved
Polar contactL521L521Preserved
Van der WaalsY513Gained
Van der WaalsF515F515Preserved
Van der WaalsA519A519Preserved
HydrophobicY454Y454Preserved
HydrophobicY513Lost

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-0.89kcal/mol
Destabilising — mild
AlphaMissense
0.157
LBen
AlphaFold pLDDT
88
model confidence
Schema
Cat 4
Category 4 — Stable Fold, Function Disrupted
ΔΔG confidence: Reduced confidence · Transmembrane
  • transmembrane position; predictor benchmarked on soluble proteins

This variant sits in the transmembrane band. The stability value was computed with a predictor benchmarked on water-soluble proteins. Published benchmarks of ddG predictors on membrane proteins report correlation below 0.4. Treat the magnitude as unreliable and the sign as weak evidence only.

Do not rank this value against a variant from a different region on ΔΔG alone.

Clinical Evidence

ClinVar classificationConflicting classifications of pathogenicity
Review statuscriteria provided, conflicting classifications
Associated conditionsWolfram-like syndrome; Cataract 41; Autosomal dominant nonsyndromic hearing loss 6 (DFNA6)
InheritanceMulti-phenotype.
Population frequency (gnomAD v4)Ultra-rare · AF 0.0040%
cDNA changec.1549C>T
ClinVar accessionVCV001396272
Last evaluated2025/04/15 00:00

Observed at very low frequency in gnomAD.

Classified for1★ unverified submission

ClinVar classifies this variant as Conflicting classifications of pathogenicity for Wolfram-like syndrome (autosomal dominant, OMIM 614296); Cataract 41 (autosomal dominant, OMIM 116400); Nonsyndromic hearing loss (DFNA6/14/38) (autosomal dominant, OMIM 600965); WFS1-related diabetes (autosomal dominant); Wolfram syndrome (classic) (autosomal recessive, OMIM 222300). These are two clinically distinct disease families: classic Wolfram syndrome requires two affected copies, while the dominant WFS1-related disorders do not. One label covers both, and it does not tell you which applies to a given person.

  • Wolfram-like syndromeautosomal dominant · OMIM 614296submitted as: Wolfram-like syndrome
  • Cataract 41autosomal dominant · OMIM 116400submitted as: Cataract 41
  • Nonsyndromic hearing loss (DFNA6/14/38)autosomal dominant · OMIM 600965submitted as: Autosomal dominant nonsyndromic hearing loss 6; Autosomal dominant nonsyndromic hearing loss 6
  • WFS1-related diabetesautosomal dominantsubmitted as: Type 2 diabetes mellitus
  • Wolfram syndrome (classic)autosomal recessive · OMIM 222300submitted as: Wolfram syndrome 1; Wolfram syndrome 1
  • Submitters conflict on this classification (1★). Treat the conditions above as submitted, not as documented phenotypes.
  • Phenotype scope is interpretation of submitted records. The computed values on this card (AlphaMissense, DynaMut2 ΔΔG, pLDDT) are measurements of the model, not of a patient.
  • Presentation cannot be generalised from neighbouring variants: one nucleotide over can present very differently. Structural similarity supports a mechanistic hypothesis, never a phenotype claim.

Review status: 1★ conflicting classifications. ClinVar "conditions" is the union of all submissions; 0–1★ entries are submitted conditions, not documented phenotypes.

Population frequency
Global (all ancestries)
AF 0.0040% · 65 / 1,612,138 alleles
Homozygotes
0
Highest-frequency population
African / African American · AF 0.0080%

Highest in African / African American: AF 0.0080% (6 of 74,950 alleles), in line with the global figure.

No homozygotes reported in gnomAD v4. For a recessive allele this is expected and is not, on its own, evidence either way.

Ancestry groupAllele freq.AC / ANHom.Carrier est.
African / African American0.0080%6 / 74,9500~1 in 6250
East Asian0.0067%3 / 44,8940~1 in 7480
Admixed American0.0050%3 / 60,0140~1 in 10000
Remaining individuals0.0048%3 / 62,4700~1 in 10410
European (non-Finnish)0.0041%48 / 1,180,0220~1 in 12290
South Asian0.0022%2 / 91,0900~1 in 22770

Source: gnomAD r4, retrieved 2026-08-21. Values are allele frequencies. The carrier estimate is derived from the allele frequency (Hardy-Weinberg, ~2·AF) and is an approximation, not a published figure — where a published carrier frequency exists it outranks this column and is cited on the card.

Structural Context

Position 517 in connecting loop, immediately upstream of M518 (M518I, M518K). Neighbors: MET518 (2.5 Å — M518 multi-variant position!), PHE516 (2.5 Å), LEU514 (3.7 Å).

R517C removes positive charge from the local environment. The M518 multi-variant position (M518I, M518K) and now R517C converge on the 514-521 loop region. AM 0.16 under-call; multi-phenotype confirms.

Amino-acid chemistry
Arginine (R) → Cysteine (C) — charge loss + thiol introduction.
Position in the protein
Connecting loop · position 517 (pLDDT 88).

Druggability Assessment

Category 3/4 — Most Druggable (AM under-call). |ΔΔG| 0.89. AlphaMissense 0.16 below threshold but THREE phenotypes confirm pathogenicity.

Mechanism: charge loss + thiol in M518 multi-variant cluster. Therapeutic: same 514-521 loop as M518I/K.

Why this matters

R517C + M518I + M518K — three variants in adjacent positions converge.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the R517C PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download R517C PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin