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R805W

Category 4 — Stable Fold, Function DisruptedConflictingLumenal · predictedσ-1 candidateEditorial
ArginineTryptophan at position 805 · C-terminal lumenal domain (653-869) · WFS1 (Wolframin)

Arginine → Tryptophan at position 805 in lumenal domain. ClinVar Conflicting. AlphaMissense 0.487 (borderline), ΔΔG +0.26 STABILISING. R→W class — aromatic replaces charge.

Interactive 3D Structure

Wild-type reference
Wild-type R805 — ionic bond to E776
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DynaMut2 mutant · R805W
Mutant W805 — ionic bond contact to E776 lost
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Bond changes · DynaMut2 interaction analysis

1 lost3 gained10 preserved
Interaction typeWild-type partnerMutant partnerStatus
Ionic bondE776Lost
Hydrogen bondF775F775Preserved
Hydrogen bondE776Gained
Hydrogen bondF840F840Preserved
Hydrogen bondE841E841Preserved
Hydrogen bondL842L842Preserved
Polar contactF775F775Preserved
Polar contactE776E776Preserved
Polar contactF840F840Preserved
Polar contactL842L842Preserved
Van der WaalsE776Gained
Van der WaalsV839Gained
HydrophobicE776E776Preserved
HydrophobicV839V839Preserved

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
0.26kcal/mol
Stabilising — mild
AlphaMissense
0.487
Amb
AlphaFold pLDDT
91
model confidence
Schema
Cat 4
Category 4 — Stable Fold, Function Disrupted
ΔΔG confidence: Standard confidence · Lumenal

This variant is in a water-facing region, which is the regime the stability predictor was built and benchmarked for. Ordinary predictor error still applies.

Clinical Evidence

ClinVar classificationConflicting classifications of pathogenicity
Review statuscriteria provided, conflicting classifications
Associated conditions(no specific conditions catalogued)
InheritanceNot specified.
Population frequency (gnomAD v4)Ultra-rare · AF 0.0022%
cDNA changec.2413C>T
ClinVar accessionVCV001675945
Last evaluated2024/10/28 00:00

Observed at very low frequency in gnomAD.

Classified for1★ unverified submission

ClinVar classifies this variant as Conflicting classifications of pathogenicity, but does not state what it is classified for. ClinVar records the condition only as "not provided". A classification without a phenotype and an inheritance mode cannot be read as a statement about Wolfram syndrome risk or severity.

  • Phenotype scope is interpretation of submitted records. The computed values on this card (AlphaMissense, DynaMut2 ΔΔG, pLDDT) are measurements of the model, not of a patient.
  • Presentation cannot be generalised from neighbouring variants: one nucleotide over can present very differently. Structural similarity supports a mechanistic hypothesis, never a phenotype claim.

Review status: 1★ conflicting classifications. ClinVar "conditions" is the union of all submissions; 0–1★ entries are submitted conditions, not documented phenotypes.

Population frequency
Global (all ancestries)
AF 0.0022% · 35 / 1,610,984 alleles
Homozygotes
1
Highest-frequency population
Admixed American · AF 0.0050%

Highest in Admixed American: AF 0.0050% (3 of 59,972 alleles), 2.3x the global figure. The global AF describes the general population, not the at-risk group.

1 homozygote reported in gnomAD v4 (1 Admixed American). gnomAD excludes individuals with severe pediatric disease, so homozygotes in this dataset argue against a fully penetrant severe recessive phenotype and belong in the clinical picture. This is interpretive signal, not a classification.

Ancestry groupAllele freq.AC / ANHom.Carrier est.
Middle Eastern · under-sampled0.016%1 / 6,0780
Admixed American0.0050%3 / 59,9721~1 in 10000
Finnish0.0048%3 / 62,3140~1 in 10390
East Asian0.0045%2 / 44,8640~1 in 11220
African / African American0.0040%3 / 74,9180~1 in 12490
European (non-Finnish)0.0019%22 / 1,178,9980~1 in 26800
South Asian · under-sampled0.0011%1 / 90,9920

Source: gnomAD r4, retrieved 2026-08-21. Values are allele frequencies. The carrier estimate is derived from the allele frequency (Hardy-Weinberg, ~2·AF) and is an approximation, not a published figure — where a published carrier frequency exists it outranks this column and is cited on the card.

Structural Context

Position 805 in lumenal domain. Neighbors: ALA806 (2.4 Å — A806P), LEU804 (2.5 Å — L804P!), PHE775 (3.4 Å — F775V!), PHE840 (3.7 Å).

R805 sits in the dense 804-806 cluster (with L804P, A806P) and contacts F775 (F775V). Replacing R805 with tryptophan eliminates the positive charge and creates a tryptophan-phenylalanine aromatic cluster with F775 + F840. The variant fold packs efficiently (+0.26).

AM 0.487 borderline; ClinVar Conflicting. The mechanism is loss of R805 charge from the F775-R805 ionic/cation-π contact discussed in F775V Atlas card.

Amino-acid chemistry
Arginine (R) → Tryptophan (W) — long positively-charged guanidinium replaced by bulky aromatic indole.
Position in the protein
C-terminal lumenal domain · position 805 (pLDDT 91).

Druggability Assessment

Category 4 — Stable Fold, Function Disrupted. ΔΔG = +0.26 stabilising. AlphaMissense 0.487 borderline.

Mechanism: loss of R805 cation-π contribution to F775 contact. Therapeutic: same 775-806 microregion (with L804P, A806P, F775V).

Why this matters

R805W is the fifth variant in the dense 775-806 microregion.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the R805W PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download R805W PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Topological domain653869 · Lumenal