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R818C

Category 4 — Stable Fold, Function DisruptedConflictingLumenal · predictedσ-1 candidateEditorial
ArginineCysteine at position 818 · C-terminal lumenal domain (653-869) · WFS1 (Wolframin)

Arginine → Cysteine at position 818 in lumenal domain. ClinVar Conflicting including monogenic diabetes + WFS1 spectrum. AlphaMissense 0.38 (below threshold), DynaMut2 ΔΔG +0.24 kcal/mol (mild stabilising). Another R→C class variant with free-thiol risk.

Interactive 3D Structure

Wild-type reference
Wild-type R818 — hydrogen bond to S821
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DynaMut2 mutant · R818C
Mutant C818 — polar contact to G820 lost (2 contacts lost)
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Bond changes · DynaMut2 interaction analysis

2 lost0 gained5 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondF704F704Preserved
Hydrogen bondS821S821Preserved
Polar contactF704F704Preserved
Polar contactG820Lost
Polar contactS821S821Preserved
Van der WaalsF704Lost
Van der WaalsS821S821Preserved

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
0.24kcal/mol
Stabilising — mild
AlphaMissense
0.382
Amb
AlphaFold pLDDT
86
model confidence
Schema
Cat 4
Category 4 — Stable Fold, Function Disrupted
ΔΔG confidence: Standard confidence · Lumenal

This variant is in a water-facing region, which is the regime the stability predictor was built and benchmarked for. Ordinary predictor error still applies.

Clinical Evidence

ClinVar classificationConflicting classifications of pathogenicity
Review statuscriteria provided, conflicting classifications
Associated conditionsMonogenic diabetes; WFS1-Related Spectrum Disorders
InheritanceMulti-phenotype.
Population frequency (gnomAD v4)Low frequency · AF 0.507%
cDNA changec.2452C>T
ClinVar accessionVCV000130748
Last evaluated2026/02/01 00:00

Observed in the general population.

Classified for1★ unverified submission

ClinVar classifies this variant as Conflicting classifications of pathogenicity for WFS1-related diabetes (autosomal dominant); WFS1-related spectrum (unresolved mode) (dominant or recessive); Wolfram syndrome (classic) (autosomal recessive, OMIM 222300); Nonsyndromic hearing loss (DFNA6/14/38) (autosomal dominant, OMIM 600965). ClinVar records this under a WFS1-spectrum label that spans both disease families — recessive Wolfram syndrome (biallelic) and the dominant WFS1-related disorders. The label does not resolve which applies, and it is not a severity statement.

  • WFS1-related diabetesautosomal dominantsubmitted as: Monogenic diabetes
  • WFS1-related spectrum (unresolved mode)dominant or recessivesubmitted as: WFS1-Related Spectrum Disorders
  • Wolfram syndrome (classic)autosomal recessive · OMIM 222300submitted as: Wolfram syndrome 1
  • Nonsyndromic hearing loss (DFNA6/14/38)autosomal dominant · OMIM 600965submitted as: Autosomal dominant nonsyndromic hearing loss 6
  • Submitters conflict on this classification (1★). Treat the conditions above as submitted, not as documented phenotypes.
  • Phenotype scope is interpretation of submitted records. The computed values on this card (AlphaMissense, DynaMut2 ΔΔG, pLDDT) are measurements of the model, not of a patient.
  • Presentation cannot be generalised from neighbouring variants: one nucleotide over can present very differently. Structural similarity supports a mechanistic hypothesis, never a phenotype claim.

Review status: 1★ conflicting classifications. ClinVar "conditions" is the union of all submissions; 0–1★ entries are submitted conditions, not documented phenotypes.

Population frequency
Global (all ancestries)
AF 0.507% · 8,135 / 1,605,064 alleles
Homozygotes
35
Highest-frequency population
Ashkenazi Jewish · AF 2.81%

Highest in Ashkenazi Jewish: AF 2.81% (826 of 29,378 alleles), 5.5x the global figure. The global AF describes the general population, not the at-risk group.

35 homozygotes reported in gnomAD v4 (8 Ashkenazi Jewish; 1 Middle Eastern; 9 South Asian; 1 Remaining individuals; 16 European (non-Finnish)). gnomAD excludes individuals with severe pediatric disease, so homozygotes in this dataset argue against a fully penetrant severe recessive phenotype and belong in the clinical picture. This is interpretive signal, not a classification.

Ancestry groupAllele freq.AC / ANHom.Carrier est.
Ashkenazi Jewish2.81%826 / 29,3788~1 in 18
Middle Eastern1.08%65 / 6,0381~1 in 46
South Asian0.765%694 / 90,7509~1 in 65
Remaining individuals0.589%366 / 62,1281~1 in 85
European (non-Finnish)0.503%5,911 / 1,174,28616~1 in 99
Finnish0.187%116 / 62,1340~1 in 270
Admixed American0.181%108 / 59,8280~1 in 280
African / African American0.063%47 / 74,9040~1 in 800
East Asian0.0045%2 / 44,7060~1 in 11180

Source: gnomAD r4, retrieved 2026-08-21. Values are allele frequencies. The carrier estimate is derived from the allele frequency (Hardy-Weinberg, ~2·AF) and is an approximation, not a published figure — where a published carrier frequency exists it outranks this column and is cited on the card.

Structural Context

Position 818 sits in wolframin's C-terminal lumenal domain. Neighbors: GLN819 (2.4 Å — same Q819 contacted by K705N/E across the fold!), LEU817 (2.5 Å), SER821 (4.4 Å — same S821 contacted by R703C across the fold). The Q819 and S821 contacts are structurally significant — R818 sits in a long-range contact network with the R705-Q819 microregion.

Replacing R818 with cysteine eliminates the positive charge contributing to the Q819 contact and introduces a free thiol into the oxidizing ER lumen. The new C818 could engage in aberrant disulfide chemistry with nearby cysteines (no immediate cysteine partners within 5 Å, but the lumenal domain has multiple cysteines that could be reached).

The ΔΔG of +0.24 is mild stabilising — the fold packs efficiently with the smaller cysteine. AlphaMissense's 0.38 is below threshold (AM under-call). Multi-phenotype clinical evidence (monogenic diabetes + WFS1 spectrum) does not resolve pathogenicity (ClinVar: conflicting submissions).

Amino-acid chemistry
Arginine (R) → Cysteine (C) — long positively-charged guanidinium replaced by short thiol-bearing residue. Loss of charge plus introduction of potential aberrant disulfide site.
Position in the protein
C-terminal lumenal domain · position 818 in the ER lumen (pLDDT 86).

Druggability Assessment

Category 4 — Stable Fold, Function Disrupted (AM under-call). ΔΔG +0.24 stabilising. AlphaMissense 0.38 below threshold and multi-phenotype clinical does not resolve it (ClinVar: conflicting submissions).

Mechanism: loss of R818 charge from Q819-S821 long-range contact network + free-thiol introduction with aberrant disulfide risk. Therapeutic strategy: site-directed at the Q819 microregion (shared with K705N/E).

Why this matters

R818C joins the growing R→C disulfide-risk class. The Q819 long-range contact links this variant to the K705 region — convergent multi-variant target.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the R818C PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download R818C PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Topological domain653869 · Lumenal
Natural variant818818 · in WFS1; dbSNP:rs35932623