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R868H

Category 4 — Stable Fold, Function DisruptedConflictingLumenal · predictedσ-1 candidateEditorial
ArginineHistidine at position 868 · C-terminal lumenal domain (653-869) · WFS1 (Wolframin)

Arginine → Histidine at position 868 near the lumenal C-terminus. ClinVar Conflicting including WFS1 spectrum. AlphaMissense 0.19 (below threshold) — AM under-call. DynaMut2 ΔΔG -0.72. pLDDT 68 borderline.

Interactive 3D Structure

Wild-type reference
Wild-type R868 — hydrogen bond to H872
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DynaMut2 mutant · R868H
Mutant H868 — polar contact contact to H872 lost
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Bond changes · DynaMut2 interaction analysis

1 lost1 gained5 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondH872H872Preserved
Polar contactD866D866Preserved
Polar contactH872H872Preserved
Aromatic / πH872Gained
Van der WaalsD866D866Preserved
Van der WaalsT870Lost
Van der WaalsH872H872Preserved

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-0.72kcal/mol
Destabilising — mild
AlphaMissense
0.191
LBen
AlphaFold pLDDT
68
model confidence
Schema
Cat 4
Category 4 — Stable Fold, Function Disrupted
ΔΔG confidence: Reduced confidence · Lumenal
  • pLDDT 67.62 below 70

The underlying AlphaFold model has pLDDT below 70 at this position, so the structure the stability calculation was run on is itself uncertain.

Do not rank this value against a variant from a different region on ΔΔG alone.

Clinical Evidence

ClinVar classificationConflicting classifications of pathogenicity
Review statuscriteria provided, conflicting classifications
Associated conditionsInborn genetic diseases; WFS1-Related Spectrum Disorders
InheritanceWFS1 spectrum.
Population frequency (gnomAD v4)Ultra-rare · AF 0.0077%
cDNA changec.2603G>A
ClinVar accessionVCV000215403
Last evaluated2025/12/10 00:00

Observed at very low frequency in gnomAD.

Classified for1★ unverified submission

ClinVar classifies this variant as Conflicting classifications of pathogenicity for WFS1-related spectrum (unresolved mode) (dominant or recessive); Wolfram syndrome (classic) (autosomal recessive, OMIM 222300); Cataract 41 (autosomal dominant, OMIM 116400); Nonsyndromic hearing loss (DFNA6/14/38) (autosomal dominant, OMIM 600965); WFS1-related diabetes (autosomal dominant); Wolfram-like syndrome (autosomal dominant, OMIM 614296). ClinVar records this under a WFS1-spectrum label that spans both disease families — recessive Wolfram syndrome (biallelic) and the dominant WFS1-related disorders. The label does not resolve which applies, and it is not a severity statement.

  • WFS1-related spectrum (unresolved mode)dominant or recessivesubmitted as: WFS1-Related Spectrum Disorders
  • Wolfram syndrome (classic)autosomal recessive · OMIM 222300submitted as: Wolfram syndrome 1; Wolfram syndrome 1
  • Cataract 41autosomal dominant · OMIM 116400submitted as: Cataract 41
  • Nonsyndromic hearing loss (DFNA6/14/38)autosomal dominant · OMIM 600965submitted as: Autosomal dominant nonsyndromic hearing loss 6; Autosomal dominant nonsyndromic hearing loss 6
  • WFS1-related diabetesautosomal dominantsubmitted as: Type 2 diabetes mellitus
  • Wolfram-like syndromeautosomal dominant · OMIM 614296submitted as: Wolfram-like syndrome
  • Submitters conflict on this classification (1★). Treat the conditions above as submitted, not as documented phenotypes.
  • Also submitted under Autistic behavior — outside the established WFS1 phenotype families; recorded here as a submission, not presented as a WFS1 phenotype.
  • Phenotype scope is interpretation of submitted records. The computed values on this card (AlphaMissense, DynaMut2 ΔΔG, pLDDT) are measurements of the model, not of a patient.
  • Presentation cannot be generalised from neighbouring variants: one nucleotide over can present very differently. Structural similarity supports a mechanistic hypothesis, never a phenotype claim.

Review status: 1★ conflicting classifications. ClinVar "conditions" is the union of all submissions; 0–1★ entries are submitted conditions, not documented phenotypes.

Population frequency
Global (all ancestries)
AF 0.0077% · 124 / 1,613,028 alleles
Homozygotes
0
Highest-frequency population
Middle Eastern · AF 0.049%

Highest in Middle Eastern: AF 0.049% (3 of 6,084 alleles), 6.4x the global figure. The global AF describes the general population, not the at-risk group.

No homozygotes reported in gnomAD v4. For a recessive allele this is expected and is not, on its own, evidence either way.

Ancestry groupAllele freq.AC / ANHom.Carrier est.
Middle Eastern0.049%3 / 6,0840~1 in 1010
South Asian0.021%19 / 91,0860~1 in 2400
Remaining individuals0.014%9 / 62,4760~1 in 3470
East Asian0.011%5 / 44,8860~1 in 4490
European (non-Finnish)0.0069%82 / 1,180,0460~1 in 7200
African / African American0.0067%5 / 74,9440~1 in 7490
Ashkenazi Jewish · under-sampled0.0034%1 / 29,6000

Source: gnomAD r4, retrieved 2026-08-21. Values are allele frequencies. The carrier estimate is derived from the allele frequency (Hardy-Weinberg, ~2·AF) and is an approximation, not a published figure — where a published carrier frequency exists it outranks this column and is cited on the card.

Structural Context

Position 868 near C-terminus. Neighbors: SER869 (2.5 Å), TRP867 (2.5 Å — W867 in TM11 cluster), ASP866 (4.0 Å — D866N region).

R868H sits in the dense 866-876 C-terminal microregion (with D866N, K876T, K862N, E864K). Partial charge loss + perturbed D866 salt-bridge contact. AM 0.19 under-call; multi-phenotype does not resolve it (ClinVar: conflicting submissions).

Amino-acid chemistry
Arginine (R) → Histidine (H) — charge partial-reduction.
Position in the protein
C-terminal lumenal domain · position 868 (pLDDT 68 borderline).

Druggability Assessment

Category 3/4 — Most Druggable (AM under-call). |ΔΔG| 0.72. AlphaMissense 0.19 below threshold and multi-phenotype does not resolve it (ClinVar: conflicting submissions).

Mechanism: partial charge loss in C-terminal multi-variant cluster. Therapeutic: same 866-876 microregion as D866N, K862N, E864K, K876T.

Why this matters

R868H extends C-terminal cluster — now 6+ variants converging.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the R868H PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download R868H PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Topological domain653869 · Lumenal