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V503G

Category 4 — Stable Fold, Function DisruptedConflictingTransmembrane · predictedEditorial
ValineGlycine at position 503 · TM6 (496-516), helical transmembrane · WFS1 (Wolframin)

Valine → Glycine at position 503 inside TM6. ClinVar Pathogenic for DFNA6 hearing loss. AlphaMissense 0.38 (below threshold) — AM under-call. DynaMut2 ΔΔG -1.88 kcal/mol — close to Cat 2 boundary. Cavity creation in dense TM6 multi-variant cluster.

Interactive 3D Structure

Wild-type reference
Wild-type V503 — hydrogen bond to L506
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DynaMut2 mutant · V503G
Mutant G503 — hydrogen bond to L484 lost (5 contacts lost)
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Bond changes · DynaMut2 interaction analysis

5 lost1 gained5 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondL484Lost
Hydrogen bondL506L506Preserved
Hydrogen bondL507L507Preserved
Polar contactL484Lost
Polar contactC505C505Preserved
Polar contactL506L506Preserved
Polar contactL507L507Preserved
Van der WaalsC505Gained
Van der WaalsL506Lost
HydrophobicL468Lost
HydrophobicF488Lost

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-1.88kcal/mol
Destabilising — moderate
AlphaMissense
0.377
Amb
AlphaFold pLDDT
81
model confidence
Schema
Cat 4
Category 4 — Stable Fold, Function Disrupted

Clinical Evidence

ClinVar classificationConflicting classifications of pathogenicity
Review statuscriteria provided, conflicting classifications
Associated conditionsAutosomal dominant nonsyndromic hearing loss 6 (DFNA6)
InheritanceAutosomal dominant DFNA6 hearing loss documented.
Population frequency (gnomAD v4)Ultra-rare · AF 0.0014%
cDNA changec.1508T>G
ClinVar accessionVCV002501448
Last evaluated2026/01/07 00:00

Observed at very low frequency in gnomAD.

Structural Context

Position 503 sits in TM6, immediately upstream of P504 (P504L Atlas card) and C505 (C505Y, Y508C Atlas region). Neighbors: SER502 (2.5 Å), PRO504 (2.5 Å), CYS505 (4.3 Å). The TM6 mid-helix region is now extensively characterized in the Atlas — V503G, P504L, C505Y, Y508C all converge here.

Replacing V503 with glycine eliminates the branched aliphatic side chain entirely, creating a substantial cavity in the bilayer-embedded core. The local packing — sized for valine + the surrounding P504 backbone constraint — cannot fill the void without local rearrangement. The TM6-TM11 register through the C505/P885 cross-helix contact (discussed in C505Y, P885L Atlas cards) is perturbed.

The |ΔΔG| of 1.88 — close to the Cat 2 moderate-destabilization threshold — reflects substantial structural cost. AlphaMissense's 0.38 is below the 0.564 pathogenic threshold (AM under-call), but the documented DFNA6 hearing loss plus the substantial ΔΔG confirm pathogenicity.

Amino-acid chemistry
Valine (V) → Glycine (G) — branched aliphatic hydrophobic replaced by smallest amino acid (no side chain). Loss of packing volume entirely.
Position in the protein
TM6 (residues 496–516) · position 503 mid-helix, bilayer-embedded (pLDDT 81).

Druggability Assessment

Category 3/4 — Most Druggable (near Cat 2 boundary, AM under-call). |ΔΔG| = 1.88 — closest to Cat 2 threshold in this batch. AlphaMissense 0.38 below threshold but DFNA6 + substantial ΔΔG confirm pathogenicity.

Mechanism: hydrophobic cavity creation in TM6 plus perturbation of the TM6-TM11 cross-helix register. Therapeutic strategy: same TM6 mid-helix microregion as P504L, C505Y, Y508C — pharmacological chaperone screening warranted given near-Cat-2 stability cost.

Why this matters

V503G is the FOURTH variant in the TM6 mid-helix cluster (with P504L, C505Y, Y508C). All converge on the same therapeutic target geometry. The proximity to P885 (TM11) through the C505 contact means this cluster connects to the TM11 multi-variant region as well — drug discovery here has unusually broad rescue convergence.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the V503G PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download V503G PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Transmembrane496516 · Helical