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V536E

Category 3/4 — Most DruggableConflictingTransmembrane · predictedEditorial
ValineGlutamate at position 536 · TM7 (529-549), helical transmembrane · WFS1 (Wolframin)

Valine → Glutamate at position 536 inside wolframin's seventh transmembrane helix (TM7). ClinVar carries conflicting classifications. AlphaMissense 0.980, DynaMut2 ΔΔG -1.62 kcal/mol (destabilising). A charge-into-membrane variant with a stronger structural cost than the typical TM-helix substitution.

Interactive 3D Structure

Wild-type reference
Wild-type V536 — hydrogen bond to P533
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DynaMut2 mutant · V536E
Mutant E536 — hydrogen bond to V532 lost (2 contacts lost)
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Bond changes · DynaMut2 interaction analysis

2 lost6 gained9 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondY405Gained
Hydrogen bondV532V532Preserved
Hydrogen bondP533P533Preserved
Hydrogen bondW540W540Preserved
Polar contactY405Gained
Polar contactF408Gained
Polar contactV532V532Preserved
Polar contactP533P533Preserved
Polar contactY534Y534Preserved
Polar contactM539Lost
Polar contactW540W540Preserved
Van der WaalsY405Gained
Van der WaalsF408Gained
Van der WaalsP533Gained
HydrophobicT361Lost
HydrophobicY405Y405Preserved
HydrophobicF408F408Preserved

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-1.62kcal/mol
Destabilising — moderate
AlphaMissense
0.980
LPath
AlphaFold pLDDT
91
model confidence
Schema
Cat 3/4
Category 3/4 — Most Druggable

Clinical Evidence

ClinVar classificationConflicting classifications of pathogenicity
Review statuscriteria provided, conflicting classifications
Associated conditionsWolfram syndrome 1
InheritanceDocumented in association with Wolfram syndrome 1 (AR). Conflicting ClinVar classifications suggest context-dependent functional consequence.
Population frequency (gnomAD v4)Absent from gnomAD v4
cDNA changec.1607T>A
ClinVar accessionVCV000432354
Last evaluated2024/05/31 00:00

Not observed in ~730k individuals — consistent with a rare allele (ACMG PM2_supporting).

Structural Context

Position 536 sits in the middle of TM7. The AlphaFold model places V536 within 5 Å of CYS537 (2.5 Å), LEU535 (2.5 Å), PHE408 (3.7 Å, from TM3 — TM3-TM7 cross-helix contact), PRO533 (3.8 Å), TYR534 (4.2 Å), and VAL532 (4.3 Å). The wild-type valine's small branched hydrophobic side chain packs into a hydrophobic environment dominated by aromatic and aliphatic residues, including the cross-helix contact to PHE408 in TM3.

Replacing valine with glutamate at this position is energetically costly. Glutamate's carboxylate group is negatively charged at physiological pH; carrying that charge into the bilayer hydrophobic core requires significant local rearrangement to position the charge near water or polar headgroups. The side chain volume is also larger than valine's, so even before considering electrostatics the local packing has to accommodate more mass.

DynaMut2 returns |ΔΔG| = 1.62 kcal/mol — the highest in this batch and approaching the Category 2 threshold (|ΔΔG| ≥ 2). The fold survives, but the energetic cost is substantial. The TM3-TM7 cross-helix interface at the PHE408 contact is particularly affected: the carboxylate's polarity is incompatible with the aromatic-hydrophobic packing the wild-type maintained.

The conflicting ClinVar classifications likely reflect the variant's mechanism-dependent functional consequence. In one cellular context (e.g., heterozygous expression where the partner allele compensates) the variant may produce mild phenotype; in homozygous or compound-heterozygous context it likely produces full Wolfram syndrome 1. AlphaMissense's score of 0.980 reflects the variant's high pathogenic potential when context allows.

Amino-acid chemistry
Valine (V) → Glutamate (E) — a small, branched hydrophobic residue replaced by a negatively-charged carboxylate-bearing residue. The chemistry shift in a bilayer-embedded position is severe.
Position in the protein
TM7 (residues 529–549) · position 536 is bilayer-embedded near the middle of the helix. The lipid environment penalizes carboxylate charge heavily.

Druggability Assessment

Category 3/4 — Most Druggable. |ΔΔG| = 1.62 kcal/mol — closest to the Category 2 threshold in this batch but still in the fold-intact range. AlphaMissense 0.980 confirms severe functional consequence.

The mechanism is charge-into-membrane disruption at the TM3-TM7 cross-helix interface (PHE408 at 3.7 Å). The introduced carboxylate is incompatible with the hydrophobic packing the wild-type valine maintained, and the helix-helix register is perturbed.

Therapeutic strategy: a small molecule that stabilizes the TM3-TM7 interface at the PHE408/V536 contact. Alternative: a pharmacological chaperone that biases the fold against the variant's locally rearranged geometry. The closer-to-Cat-2 |ΔΔG| suggests chaperone screening may be a more accessible approach than purely site-directed binders.

Why this matters

V536E exemplifies the boundary between Category 3/4 (site-directed binders) and Category 2 (chaperones) in the Atlas schema. With |ΔΔG| of 1.62, the variant sits in the most-druggable tier but close enough to the moderate-destabilization threshold that chaperone screening is justified alongside site-directed design. The Atlas's continuous classification (rather than binary) captures variants at this boundary cleanly.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the V536E PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download V536E PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Transmembrane529549 · Helical