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V707F

Category 3/4 — Most DruggablePathogenicLumenal · predictedσ-1 candidateEditorial
ValinePhenylalanine at position 707 · C-terminal lumenal domain (653-869) · WFS1 (Wolframin)

Valine → Phenylalanine at position 707 in wolframin's C-terminal lumenal domain. ClinVar Pathogenic for classical autosomal recessive Wolfram syndrome 1. AlphaMissense 0.935, DynaMut2 ΔΔG -0.31 kcal/mol (destabilising). A conservative-to-aromatic substitution in a critical lumenal position.

Interactive 3D Structure

Wild-type reference
Wild-type V707 — hydrogen bond to E776
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DynaMut2 mutant · V707F
Mutant F707 — hydrophobic to L814 lost (3 contacts lost)
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Bond changes · DynaMut2 interaction analysis

3 lost2 gained2 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondE776E776Preserved
Aromatic / πF704Gained
HydrophobicF704F704Preserved
HydrophobicF775Lost
HydrophobicI777Lost
HydrophobicL814Lost
HydrophobicL815Gained

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-0.31kcal/mol
Destabilising — mild
AlphaMissense
0.935
LPath
AlphaFold pLDDT
92
model confidence
Schema
Cat 3/4
Category 3/4 — Most Druggable
ΔΔG confidence: Standard confidence · Lumenal

This variant is in a water-facing region, which is the regime the stability predictor was built and benchmarked for. Ordinary predictor error still applies.

Clinical Evidence

ClinVar classificationPathogenic
Review statusno assertion criteria provided
Associated conditionsWolfram syndrome 1
InheritanceAutosomal recessive Wolfram syndrome 1 phenotype documented in ClinVar.
Population frequency (gnomAD v4)Absent from gnomAD v4
cDNA changec.2119G>T
ClinVar accessionVCV000030552
Last evaluated2008/12/15 00:00

Not observed in ~730k individuals — consistent with a rare allele (ACMG PM2_supporting).

Classified for0★ unverified submission

ClinVar classifies this variant as Pathogenic for Wolfram syndrome (classic) (autosomal recessive, OMIM 222300). Classic Wolfram syndrome is recessive: a single copy does not produce it, and this classification says nothing about a carrier's own risk.

  • Wolfram syndrome (classic)autosomal recessive · OMIM 222300submitted as: Wolfram syndrome 1
  • No assertion criteria were provided (0★). Treat the conditions above as unverified submissions, not as documented phenotypes.
  • Phenotype scope is interpretation of submitted records. The computed values on this card (AlphaMissense, DynaMut2 ΔΔG, pLDDT) are measurements of the model, not of a patient.
  • Presentation cannot be generalised from neighbouring variants: one nucleotide over can present very differently. Structural similarity supports a mechanistic hypothesis, never a phenotype claim.

Review status: 0★ no assertion criteria provided. ClinVar "conditions" is the union of all submissions; 0–1★ entries are submitted conditions, not documented phenotypes.

Population frequency
Global (all ancestries)
Absent from gnomAD v4
Homozygotes
Not available

No population breakdown — the variant is absent from gnomAD v4, so no ancestry group has an observed frequency.

No homozygotes — the variant is absent from gnomAD v4 altogether.

Source: gnomAD r4, retrieved 2026-08-21. Values are allele frequencies. The carrier estimate is derived from the allele frequency (Hardy-Weinberg, ~2·AF) and is an approximation, not a published figure — where a published carrier frequency exists it outranks this column and is cited on the card.

Structural Context

Position 707 sits in wolframin's C-terminal lumenal domain. The AlphaFold model places V707 within 5 Å of ARG708 (2.4 Å), TYR706 (2.5 Å), GLU776 (3.5 Å — long-range contact), PHE704 (4.2 Å — another long-range), and ILE777 (4.5 Å). The local environment combines basic (R708), aromatic (Y706, F704), and acidic (E776) residues.

The wild-type valine at 707 provides moderate hydrophobic packing into this mixed-character pocket. The branched aliphatic side chain fits cleanly between the surrounding residues without crowding.

Replacing valine with phenylalanine introduces a substantial volume increase plus an aromatic ring system. The local pocket — sized for valine — must rearrange to accommodate the larger phenyl ring. The two nearby aromatics (Y706 at 2.5 Å, F704 at 4.2 Å) could engage in π-stacking with the new F707, creating a three-aromatic cluster that the wild-type fold did not have. Whether this rearrangement is productive (stable three-aromatic stack) or destructive (disrupting Y706/F704 contacts with their own partners) depends on the specific geometry the variant fold adopts.

The |ΔΔG| of 0.31 indicates the fold absorbs the substitution. AlphaMissense's 0.935 score reflects the functional consequence — the rearranged aromatic cluster disrupts whatever interaction the wild-type valine geometry enabled.

Amino-acid chemistry
Valine (V) → Phenylalanine (F) — a small branched hydrophobic replaced by a large aromatic. Volume increases substantially; π-electron system added where wild-type had only aliphatic carbons.
Position in the protein
C-terminal lumenal domain · position 707 in the ER lumen with high AlphaFold confidence (pLDDT 92).

Druggability Assessment

Category 3/4 — Most Druggable. |ΔΔG| = 0.31 kcal/mol — fold survives. AlphaMissense 0.935 confirms severe functional consequence.

The mechanism is local volume mismatch creating an aromatic cluster (F707 + Y706 + F704) where the wild-type valine maintained a smaller hydrophobic pocket. Therapeutic strategy: site-directed small molecules that compensate for the disrupted Y706/F704 geometry by occupying the wild-type V707 niche.

Why this matters

V707F demonstrates that classical Wolfram syndrome 1 (AR inheritance) is well-represented in the Atlas's most-druggable category. The mechanism — local volume disruption in a lumenal pocket — is straightforward and amenable to structure-based design.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the V707F PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download V707F PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Topological domain653869 · Lumenal