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L543F

Category 4 — Stable Fold, Function DisruptedLikely pathogenicTransmembrane · predictedEditorial
LeucinePhenylalanine at position 543 · TM7 (529-549), helical transmembrane · WFS1 (Wolframin)

Leucine → Phenylalanine at position 543 inside TM7. ClinVar Likely pathogenic for Wolfram syndrome 1. AlphaMissense 0.303 (below threshold) — AM under-call. DynaMut2 ΔΔG -1.34 kcal/mol (destabilising). Same position as L543P (Atlas card adjacent) but with aromatic introduction.

Interactive 3D Structure

Wild-type reference
Wild-type L543 — hydrogen bond to M539
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DynaMut2 mutant · L543F
Mutant F543 — polar contact to I547 lost (4 contacts lost)
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Bond changes · DynaMut2 interaction analysis

4 lost5 gained11 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondM539M539Preserved
Hydrogen bondV546V546Preserved
Hydrogen bondI547I547Preserved
Polar contactM539M539Preserved
Polar contactC541C541Preserved
Polar contactV545Gained
Polar contactV546V546Preserved
Polar contactI547I547Preserved
Aromatic / πF881Gained
Van der WaalsV545Gained
Van der WaalsI547Lost
HydrophobicF354Lost
HydrophobicM357M357Preserved
HydrophobicV412Gained
HydrophobicV415V415Preserved
HydrophobicI416Gained
HydrophobicT436T436Preserved
HydrophobicW540Lost
HydrophobicI547Lost
HydrophobicF881F881Preserved

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-1.34kcal/mol
Destabilising — moderate
AlphaMissense
0.303
LBen
AlphaFold pLDDT
91
model confidence
Schema
Cat 4
Category 4 — Stable Fold, Function Disrupted
ΔΔG confidence: Reduced confidence · Transmembrane
  • transmembrane position; predictor benchmarked on soluble proteins

This variant sits in the transmembrane band. The stability value was computed with a predictor benchmarked on water-soluble proteins. Published benchmarks of ddG predictors on membrane proteins report correlation below 0.4. Treat the magnitude as unreliable and the sign as weak evidence only.

Do not rank this value against a variant from a different region on ΔΔG alone.

Clinical Evidence

ClinVar classificationLikely pathogenic
Review statuscriteria provided, single submitter
Associated conditionsWolfram syndrome 1
InheritanceWolfram syndrome 1 (AR) documented.
Population frequency (gnomAD v4)Ultra-rare · AF 0.000068%
cDNA changec.1627C>T
ClinVar accessionVCV002499486
Last evaluated2023/03/01 00:00

Observed at very low frequency in gnomAD.

Classified for1★ unverified submission

ClinVar classifies this variant as Likely pathogenic for Wolfram syndrome (classic) (autosomal recessive, OMIM 222300). Classic Wolfram syndrome is recessive: a single copy does not produce it, and this classification says nothing about a carrier's own risk.

  • Wolfram syndrome (classic)autosomal recessive · OMIM 222300submitted as: Wolfram syndrome 1
  • This rests on a single submitter (1★). Treat the conditions above as submitted, not as documented phenotypes.
  • Phenotype scope is interpretation of submitted records. The computed values on this card (AlphaMissense, DynaMut2 ΔΔG, pLDDT) are measurements of the model, not of a patient.
  • Presentation cannot be generalised from neighbouring variants: one nucleotide over can present very differently. Structural similarity supports a mechanistic hypothesis, never a phenotype claim.

Review status: 1★ single submitter. ClinVar "conditions" is the union of all submissions; 0–1★ entries are submitted conditions, not documented phenotypes.

Population frequency
Global (all ancestries)
AF 0.000068% · 1 / 1,460,098 alleles
Homozygotes
0

Every ancestry group with observed alleles falls below the reporting threshold (min 2 alleles, min 500 sampled) — too sparse to name a highest-frequency population.

No homozygotes reported in gnomAD v4. For a recessive allele this is expected and is not, on its own, evidence either way.

Ancestry groupAllele freq.AC / ANHom.Carrier est.
European (non-Finnish) · under-sampled0.000090%1 / 1,111,9980

Source: gnomAD r4, retrieved 2026-08-21. Values are allele frequencies. The carrier estimate is derived from the allele frequency (Hardy-Weinberg, ~2·AF) and is an approximation, not a published figure — where a published carrier frequency exists it outranks this column and is cited on the card.

Structural Context

Position 543 sits in TM7. Same neighbor environment as L543P: GLU542 (2.5 Å), SER544 (2.5 Å), MET539 (3.7 Å), TRP540 (3.9 Å), PHE881 (4.1 Å — TM7-TM11 cross-helix).

Replacing L543 with phenylalanine adds aromatic volume to the TM7 mid-helix. Unlike L543P which introduces a backbone kink, L543F preserves α-helical structure but creates a tandem aromatic motif with W540 nearby. The TM7-TM11 cross-helix contact to F881 now involves two phenylalanines in TM7 (F543, with W540 aromatic neighbor) interacting with F881 across the interface.

The |ΔΔG| of 1.34 reflects meaningful fold cost. AlphaMissense's 0.303 below threshold is AM under-call; ClinVar Pathogenic + Wolfram 1 establishes pathogenicity.

Amino-acid chemistry
Leucine (L) → Phenylalanine (F) — branched aliphatic hydrophobic replaced by aromatic hydrophobic.
Position in the protein
TM7 (residues 529–549) · position 543 mid-helix, bilayer-embedded (pLDDT 91).

Druggability Assessment

Category 3/4 — Most Druggable (AM under-call). |ΔΔG| = 1.34 — fold survives at meaningful cost. AlphaMissense 0.303 below threshold but ClinVar Pathogenic + Wolfram 1.

Mechanism is aromatic volume mismatch in TM7 plus rearrangement of TM7-TM11 cross-helix contact. Therapeutic strategy: same TM7-TM11 interface as L543P.

Why this matters

L543F + L543P at the same position, different chemistries, both pathogenic — position 543 is a multi-substitution hotspot in TM7.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the L543F PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download L543F PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Transmembrane529549 · Helical