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L734H

Category 4 — Stable Fold, Function DisruptedConflictingLumenal · predictedσ-1 candidateEditorial
LeucineHistidine at position 734 · C-terminal lumenal domain (653-869) · WFS1 (Wolframin)

Leucine → Histidine at position 734 in lumenal domain. ClinVar Conflicting including Wolfram syndrome 1. AlphaMissense 0.461 (below threshold), ΔΔG -0.47.

Interactive 3D Structure

Wild-type reference
Wild-type L734 — hydrogen bond to W730
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DynaMut2 mutant · L734H
Mutant H734 — polar contact to W730 lost (2 contacts lost)
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Bond changes · DynaMut2 interaction analysis

2 lost0 gained4 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondW730W730Preserved
Hydrogen bondM731M731Preserved
Polar contactW730W730Preserved
Polar contactM731M731Preserved
HydrophobicW730Lost
HydrophobicM731Lost

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-0.47kcal/mol
Destabilising — mild
AlphaMissense
0.461
Amb
AlphaFold pLDDT
88
model confidence
Schema
Cat 4
Category 4 — Stable Fold, Function Disrupted
ΔΔG confidence: Standard confidence · Lumenal

This variant is in a water-facing region, which is the regime the stability predictor was built and benchmarked for. Ordinary predictor error still applies.

Clinical Evidence

ClinVar classificationConflicting classifications of pathogenicity
Review statuscriteria provided, conflicting classifications
Associated conditionsWolfram syndrome 1
InheritanceWolfram syndrome 1.
Population frequency (gnomAD v4)Absent from gnomAD v4
cDNA changec.2201T>A
ClinVar accessionVCV000593953
Last evaluated2017/09/26 00:00

Not observed in ~730k individuals — consistent with a rare allele (ACMG PM2_supporting).

Classified for1★ unverified submission

ClinVar classifies this variant as Conflicting classifications of pathogenicity for Wolfram syndrome (classic) (autosomal recessive, OMIM 222300). Classic Wolfram syndrome is recessive: a single copy does not produce it, and this classification says nothing about a carrier's own risk.

  • Wolfram syndrome (classic)autosomal recessive · OMIM 222300submitted as: Wolfram syndrome 1
  • Submitters conflict on this classification (1★). Treat the conditions above as submitted, not as documented phenotypes.
  • Phenotype scope is interpretation of submitted records. The computed values on this card (AlphaMissense, DynaMut2 ΔΔG, pLDDT) are measurements of the model, not of a patient.
  • Presentation cannot be generalised from neighbouring variants: one nucleotide over can present very differently. Structural similarity supports a mechanistic hypothesis, never a phenotype claim.

Review status: 1★ conflicting classifications. ClinVar "conditions" is the union of all submissions; 0–1★ entries are submitted conditions, not documented phenotypes.

Population frequency
Global (all ancestries)
Absent from gnomAD v4
Homozygotes
Not available

No population breakdown — the variant is absent from gnomAD v4, so no ancestry group has an observed frequency.

No homozygotes — the variant is absent from gnomAD v4 altogether.

Source: gnomAD r4, retrieved 2026-08-21. Values are allele frequencies. The carrier estimate is derived from the allele frequency (Hardy-Weinberg, ~2·AF) and is an approximation, not a published figure — where a published carrier frequency exists it outranks this column and is cited on the card.

Structural Context

Position 734 in lumenal domain — same C733-C765 disulfide region (R732C, C733G, C765R). Neighbors: TYR735 (2.5 Å — Y735 partner of G736 environment), CYS733 (2.5 Å — the C733 disulfide cysteine!), MET731 (3.8 Å), TRP730 (3.8 Å).

L734H sits immediately downstream of C733 — perturbing the C733-C765 disulfide region from the adjacent position. AM 0.461 below threshold and Wolfram 1 does not resolve it (ClinVar: conflicting submissions).

Amino-acid chemistry
Leucine (L) → Histidine (H) — branched aliphatic replaced by aromatic titratable basic.
Position in the protein
C-terminal lumenal domain · position 734 (pLDDT 88).

Druggability Assessment

Category 3/4 — Most Druggable (AM under-call). |ΔΔG| 0.47. AlphaMissense 0.461 below threshold and Wolfram 1 does not resolve it (ClinVar: conflicting submissions).

Mechanism: perturbation of C733-C765 disulfide region from adjacent position. Therapeutic: same C733-C765 microregion.

Why this matters

L734H is in the same C733-C765 disulfide microregion as R732C, C733G, C765R.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the L734H PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download L734H PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Topological domain653869 · Lumenal