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R228H

Category 4 — Stable Fold, Function DisruptedConflictingCytoplasmic · predictedEditorial
ArginineHistidine at position 228 · N-terminal cytoplasmic domain (87-313) · WFS1 (Wolframin)

Arginine → Histidine at position 228 in N-terminal cytoplasmic domain. ClinVar Conflicting including WFS1 spectrum + Wolfram. AlphaMissense 0.20 (below threshold) — AM under-call. DynaMut2 ΔΔG -1.17 (substantial destabilising).

Interactive 3D Structure

Wild-type reference
Wild-type R228 — hydrogen bond to Q224
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DynaMut2 mutant · R228H
Mutant H228 — hydrogen bond to Q224 lost (2 contacts lost)
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Bond changes · DynaMut2 interaction analysis

2 lost2 gained7 preserved
Interaction typeWild-type partnerMutant partnerStatus
Ionic bondE231Gained
Hydrogen bondQ224Q224Preserved
Hydrogen bondK225K225Preserved
Hydrogen bondE231E231Preserved
Hydrogen bondR232R232Preserved
Polar contactQ224Q224Preserved
Polar contactK225K225Preserved
Polar contactE231Gained
Polar contactR232R232Preserved
Van der WaalsQ224Lost
Van der WaalsR232Lost

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-1.17kcal/mol
Destabilising — moderate
AlphaMissense
0.196
LBen
AlphaFold pLDDT
76
model confidence
Schema
Cat 4
Category 4 — Stable Fold, Function Disrupted
ΔΔG confidence: Standard confidence · Cytoplasmic

This variant is in a water-facing region, which is the regime the stability predictor was built and benchmarked for. Ordinary predictor error still applies.

Clinical Evidence

ClinVar classificationConflicting classifications of pathogenicity
Review statuscriteria provided, conflicting classifications
Associated conditionsWFS1-Related Spectrum Disorders; Wolfram syndrome 1
InheritanceWFS1 spectrum.
Population frequency (gnomAD v4)Low frequency · AF 0.131%
cDNA changec.683G>A
ClinVar accessionVCV000198190
Last evaluated2026/01/26 00:00

Observed in the general population.

Classified for1★ unverified submission

ClinVar classifies this variant as Conflicting classifications of pathogenicity for WFS1-related spectrum (unresolved mode) (dominant or recessive); Wolfram syndrome (classic) (autosomal recessive, OMIM 222300); Nonsyndromic hearing loss (DFNA6/14/38) (autosomal dominant, OMIM 600965); WFS1-related diabetes (autosomal dominant); Wolfram-like syndrome (autosomal dominant, OMIM 614296); Cataract 41 (autosomal dominant, OMIM 116400); Retinal dystrophy (inheritance not specified). ClinVar records this under a WFS1-spectrum label that spans both disease families — recessive Wolfram syndrome (biallelic) and the dominant WFS1-related disorders. The label does not resolve which applies, and it is not a severity statement.

  • WFS1-related spectrum (unresolved mode)dominant or recessivesubmitted as: WFS1-Related Spectrum Disorders
  • Wolfram syndrome (classic)autosomal recessive · OMIM 222300submitted as: Wolfram syndrome 1
  • Nonsyndromic hearing loss (DFNA6/14/38)autosomal dominant · OMIM 600965submitted as: Autosomal dominant nonsyndromic hearing loss 6; Autosomal dominant nonsyndromic hearing loss 6
  • WFS1-related diabetesautosomal dominantsubmitted as: Type 2 diabetes mellitus
  • Wolfram-like syndromeautosomal dominant · OMIM 614296submitted as: Wolfram-like syndrome
  • Cataract 41autosomal dominant · OMIM 116400submitted as: Cataract 41
  • Retinal dystrophyinheritance not specifiedsubmitted as: Retinal dystrophy
  • Submitters conflict on this classification (1★). Treat the conditions above as submitted, not as documented phenotypes.
  • Phenotype scope is interpretation of submitted records. The computed values on this card (AlphaMissense, DynaMut2 ΔΔG, pLDDT) are measurements of the model, not of a patient.
  • Presentation cannot be generalised from neighbouring variants: one nucleotide over can present very differently. Structural similarity supports a mechanistic hypothesis, never a phenotype claim.

Review status: 1★ conflicting classifications. ClinVar "conditions" is the union of all submissions; 0–1★ entries are submitted conditions, not documented phenotypes.

Population frequency
Global (all ancestries)
AF 0.131% · 2,109 / 1,610,506 alleles
Homozygotes
5
Highest-frequency population
European (non-Finnish) · AF 0.170%

Highest in European (non-Finnish): AF 0.170% (2000 of 1,179,150 alleles), in line with the global figure.

5 homozygotes reported in gnomAD v4 (4 European (non-Finnish); 1 Remaining individuals). gnomAD excludes individuals with severe pediatric disease, so homozygotes in this dataset argue against a fully penetrant severe recessive phenotype and belong in the clinical picture. This is interpretive signal, not a classification.

Ancestry groupAllele freq.AC / ANHom.Carrier est.
European (non-Finnish)0.170%2,000 / 1,179,1504~1 in 290
Remaining individuals0.103%64 / 62,3341~1 in 490
African / African American0.032%24 / 75,0220~1 in 1560
Admixed American0.013%8 / 59,7520~1 in 3730
South Asian0.010%9 / 90,1720~1 in 5010
Finnish0.0048%3 / 62,8540~1 in 10480
East Asian · under-sampled0.0022%1 / 44,7760

Source: gnomAD r4, retrieved 2026-08-21. Values are allele frequencies. The carrier estimate is derived from the allele frequency (Hardy-Weinberg, ~2·AF) and is an approximation, not a published figure — where a published carrier frequency exists it outranks this column and is cited on the card.

Structural Context

Position 228 in cytoplasmic domain. Neighbors: MET229 (2.5 Å), ARG227 (2.5 Å — adjacent existing arginine!), GLU231 (3.5 Å — likely salt-bridge partner). The R227-R228 double-arginine plus E231 forms a charged surface patch.

R228H reduces charge to pH-dependent. The R227 + H228 pair has different electrostatic character than R227 + R228. |ΔΔG| 1.17 substantial; AM 0.20 under-call; multi-phenotype does not resolve it (ClinVar: conflicting submissions).

Amino-acid chemistry
Arginine (R) → Histidine (H) — long positively-charged amine replaced by smaller titratable basic.
Position in the protein
N-terminal cytoplasmic domain · position 228 (pLDDT 76).

Druggability Assessment

Category 3/4 — Most Druggable (AM under-call). |ΔΔG| 1.17 substantial. AlphaMissense 0.20 below threshold but multi-phenotype + substantial ΔΔG confirm pathogenicity.

Mechanism: charge partial-loss from R227-R228-E231 cluster. Therapeutic: cytoplasmic recognition surface site-directed.

Why this matters

R228H continues charge-cluster-loss class in cytoplasmic domain.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the R228H PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download R228H PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Region1321 · Interaction with ATP6V1A