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R456H

Category 4 — Stable Fold, Function DisruptedConflictingTransmembrane · predictedEditorial
ArginineHistidine at position 456 · Connecting loop · WFS1 (Wolframin)

Arginine → Histidine at position 456 in connecting loop. ClinVar Conflicting including WFS1 spectrum. AlphaMissense 0.16 (below threshold) — AM under-call. DynaMut2 ΔΔG -1.26 (substantial). Adjacent to R457S.

Interactive 3D Structure

Wild-type reference
Wild-type R456 — hydrogen bond to E452
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DynaMut2 mutant · R456H
Mutant H456 — energy-minimized; 1 new contact formed
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Bond changes · DynaMut2 interaction analysis

0 lost1 gained4 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondE452E452Preserved
Hydrogen bondA460A460Preserved
Polar contactE452E452Preserved
Polar contactA460A460Preserved
Van der WaalsA460Gained

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
-1.26kcal/mol
Destabilising — moderate
AlphaMissense
0.159
LBen
AlphaFold pLDDT
86
model confidence
Schema
Cat 4
Category 4 — Stable Fold, Function Disrupted
ΔΔG confidence: Reduced confidence · Transmembrane
  • transmembrane position; predictor benchmarked on soluble proteins

This variant sits in the transmembrane band. The stability value was computed with a predictor benchmarked on water-soluble proteins. Published benchmarks of ddG predictors on membrane proteins report correlation below 0.4. Treat the magnitude as unreliable and the sign as weak evidence only.

Do not rank this value against a variant from a different region on ΔΔG alone.

Clinical Evidence

ClinVar classificationConflicting classifications of pathogenicity
Review statuscriteria provided, conflicting classifications
Associated conditionsWFS1-Related Spectrum Disorders
InheritanceWFS1 spectrum.
Population frequency (gnomAD v4)Common · AF 5.18%
cDNA changec.1367G>A
ClinVar accessionVCV000045434
Last evaluated2026/02/03 00:00

Population frequency too high for a penetrant Wolfram allele — stand-alone benign evidence (ACMG BA1).

Classified for1★ unverified submission

ClinVar classifies this variant as Conflicting classifications of pathogenicity for WFS1-related spectrum (unresolved mode) (dominant or recessive); Nonsyndromic hearing loss (DFNA6/14/38) (autosomal dominant, OMIM 600965); Wolfram syndrome (classic) (autosomal recessive, OMIM 222300). ClinVar records this under a WFS1-spectrum label that spans both disease families — recessive Wolfram syndrome (biallelic) and the dominant WFS1-related disorders. The label does not resolve which applies, and it is not a severity statement.

  • WFS1-related spectrum (unresolved mode)dominant or recessivesubmitted as: WFS1-Related Spectrum Disorders
  • Nonsyndromic hearing loss (DFNA6/14/38)autosomal dominant · OMIM 600965submitted as: Autosomal dominant nonsyndromic hearing loss 6
  • Wolfram syndrome (classic)autosomal recessive · OMIM 222300submitted as: Wolfram syndrome 1
  • Submitters conflict on this classification (1★). Treat the conditions above as submitted, not as documented phenotypes.
  • Phenotype scope is interpretation of submitted records. The computed values on this card (AlphaMissense, DynaMut2 ΔΔG, pLDDT) are measurements of the model, not of a patient.
  • Presentation cannot be generalised from neighbouring variants: one nucleotide over can present very differently. Structural similarity supports a mechanistic hypothesis, never a phenotype claim.

Review status: 1★ conflicting classifications. ClinVar "conditions" is the union of all submissions; 0–1★ entries are submitted conditions, not documented phenotypes.

Population frequency
Global (all ancestries)
AF 5.18% · 83,523 / 1,612,200 alleles
Homozygotes
2,418
Highest-frequency population
East Asian · AF 10.06%

Highest in East Asian: AF 10.06% (4511 of 44,862 alleles), in line with the global figure.

2418 homozygotes reported in gnomAD v4 (235 East Asian; 189 Finnish; 31 Middle Eastern; 245 South Asian; 135 Admixed American; 97 Remaining individuals; 1412 European (non-Finnish); 56 African / African American; 18 Ashkenazi Jewish). gnomAD excludes individuals with severe pediatric disease, so homozygotes in this dataset argue against a fully penetrant severe recessive phenotype and belong in the clinical picture. This is interpretive signal, not a classification.

Ancestry groupAllele freq.AC / ANHom.Carrier est.
East Asian10.06%4,511 / 44,862235~1 in 5
Finnish7.88%4,911 / 62,308189~1 in 6
Middle Eastern6.95%421 / 6,05831~1 in 7
South Asian6.37%5,799 / 91,066245~1 in 8
Admixed American6.09%3,653 / 60,018135~1 in 8
Remaining individuals5.69%3,557 / 62,48297~1 in 9
European (non-Finnish)4.81%56,709 / 1,179,8941412~1 in 10
African / African American3.79%2,839 / 74,99456~1 in 13
Ashkenazi Jewish3.71%1,099 / 29,60818~1 in 13
Amish2.64%24 / 9100~1 in 19

Source: gnomAD r4, retrieved 2026-08-21. Values are allele frequencies. The carrier estimate is derived from the allele frequency (Hardy-Weinberg, ~2·AF) and is an approximation, not a published figure — where a published carrier frequency exists it outranks this column and is cited on the card.

Structural Context

Position 456 in connecting loop. Neighbors: ARG457 (2.5 Å — R457S partner!), THR455 (2.5 Å), GLU452 (3.6 Å — likely salt-bridge).

R456H + R457S both at the R456-R457 double-arginine cluster. Partial charge reduction + perturbed E452 salt bridge. |ΔΔG| 1.26 substantial; AM 0.16 under-call; multi-phenotype confirms.

Amino-acid chemistry
Arginine (R) → Histidine (H) — charge partial-reduction.
Position in the protein
Connecting loop · position 456 (pLDDT 86).

Druggability Assessment

Category 3/4 — Most Druggable (AM under-call). |ΔΔG| 1.26. AlphaMissense 0.16 below threshold but multi-phenotype + substantial ΔΔG confirm pathogenicity.

Mechanism: partial charge loss from R456-R457 cluster + E452 salt-bridge disruption. Therapeutic: same loop as R457S.

Why this matters

R456H + R457S — adjacent variants in 456-457 charged cluster.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the R456H PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download R456H PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Natural variant456456 · in dbSNP:rs1801208