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R685C

Category 3/4 — Most DruggableConflictingLumenal · predictedσ-1 candidateEditorial
ArginineCysteine at position 685 · C-terminal lumenal domain (653-869) · WFS1 (Wolframin)

Arginine → Cysteine at position 685. ClinVar Conflicting including monogenic diabetes + DFNA6. AlphaMissense 0.581, ΔΔG +0.10. Same position as R685P (Atlas card). R→C class with disulfide-pair partner CYS673 visible nearby in the broader region.

Interactive 3D Structure

Wild-type reference
Wild-type R685 — hydrogen bond to L689
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DynaMut2 mutant · R685C
Mutant C685 — energy-minimized; 2 new contacts formed
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Bond changes · DynaMut2 interaction analysis

0 lost2 gained8 preserved
Interaction typeWild-type partnerMutant partnerStatus
Hydrogen bondN682N682Preserved
Hydrogen bondI688I688Preserved
Hydrogen bondL689L689Preserved
Polar contactN682N682Preserved
Polar contactM683M683Preserved
Polar contactI688I688Preserved
Polar contactL689L689Preserved
Van der WaalsN682Gained
Van der WaalsM683M683Preserved
HydrophobicN682Gained

Lost / gained / preserved interatomic contacts at the variant residue, from the DynaMut2 (Arpeggio) interaction analysis of the wild-type and energy-minimized mutant structures.

Computational Predictions

DynaMut2 ΔΔG
0.10kcal/mol
Stabilising — mild
AlphaMissense
0.581
LPath
AlphaFold pLDDT
90
model confidence
Schema
Cat 3/4
Category 3/4 — Most Druggable
ΔΔG confidence: Standard confidence · Lumenal

This variant is in a water-facing region, which is the regime the stability predictor was built and benchmarked for. Ordinary predictor error still applies.

Clinical Evidence

ClinVar classificationConflicting classifications of pathogenicity
Review statuscriteria provided, conflicting classifications
Associated conditionsMonogenic diabetes; Wolfram syndrome 1; Autosomal dominant nonsyndromic hearing loss 6 (DFNA6)
InheritanceMonogenic diabetes + DFNA6.
Population frequency (gnomAD v4)Low frequency · AF 0.018%
cDNA changec.2053C>T
ClinVar accessionVCV000393391
Last evaluated2026/02/17 00:00

Observed in the general population.

Classified for1★ unverified submission

ClinVar classifies this variant as Conflicting classifications of pathogenicity for WFS1-related diabetes (autosomal dominant); Wolfram syndrome (classic) (autosomal recessive, OMIM 222300); Nonsyndromic hearing loss (DFNA6/14/38) (autosomal dominant, OMIM 600965); Cataract 41 (autosomal dominant, OMIM 116400); Wolfram-like syndrome (autosomal dominant, OMIM 614296); Optic atrophy / optic neuropathy (autosomal dominant). These are two clinically distinct disease families: classic Wolfram syndrome requires two affected copies, while the dominant WFS1-related disorders do not. One label covers both, and it does not tell you which applies to a given person.

  • WFS1-related diabetesautosomal dominantsubmitted as: Monogenic diabetes; Type 2 diabetes mellitus
  • Wolfram syndrome (classic)autosomal recessive · OMIM 222300submitted as: Wolfram syndrome 1; Wolfram syndrome 1
  • Nonsyndromic hearing loss (DFNA6/14/38)autosomal dominant · OMIM 600965submitted as: Autosomal dominant nonsyndromic hearing loss 6; Autosomal dominant nonsyndromic hearing loss 6
  • Cataract 41autosomal dominant · OMIM 116400submitted as: Cataract 41
  • Wolfram-like syndromeautosomal dominant · OMIM 614296submitted as: Wolfram-like syndrome
  • Optic atrophy / optic neuropathyautosomal dominantsubmitted as: Optic atrophy
  • Submitters conflict on this classification (1★). Treat the conditions above as submitted, not as documented phenotypes.
  • Phenotype scope is interpretation of submitted records. The computed values on this card (AlphaMissense, DynaMut2 ΔΔG, pLDDT) are measurements of the model, not of a patient.
  • Presentation cannot be generalised from neighbouring variants: one nucleotide over can present very differently. Structural similarity supports a mechanistic hypothesis, never a phenotype claim.

Review status: 1★ conflicting classifications. ClinVar "conditions" is the union of all submissions; 0–1★ entries are submitted conditions, not documented phenotypes.

Population frequency
Global (all ancestries)
AF 0.018% · 288 / 1,612,938 alleles
Homozygotes
0
Highest-frequency population
Middle Eastern · AF 0.082%

Highest in Middle Eastern: AF 0.082% (5 of 6,062 alleles), 4.6x the global figure. The global AF describes the general population, not the at-risk group.

No homozygotes reported in gnomAD v4. For a recessive allele this is expected and is not, on its own, evidence either way.

Ancestry groupAllele freq.AC / ANHom.Carrier est.
Middle Eastern0.082%5 / 6,0620~1 in 610
East Asian0.056%25 / 44,8680~1 in 900
Remaining individuals0.038%24 / 62,4840~1 in 1300
South Asian0.036%33 / 91,0760~1 in 1380
African / African American0.027%20 / 75,0280~1 in 1880
Admixed American0.017%10 / 60,0320~1 in 3000
European (non-Finnish)0.014%171 / 1,179,9440~1 in 3450

Source: gnomAD r4, retrieved 2026-08-21. Values are allele frequencies. The carrier estimate is derived from the allele frequency (Hardy-Weinberg, ~2·AF) and is an approximation, not a published figure — where a published carrier frequency exists it outranks this column and is cited on the card.

Structural Context

Position 685 same neighbors as R685P: THR686 (2.5 Å), ALA684 (2.5 Å — A684T/V/G cluster), ASN682 (3.5 Å), MET683 (4.3 Å), GLN687 (4.4 Å — Q687H).

R685C is a second pathogenic substitution at 685. Where R685P removed charge + introduced backbone kink, R685C removes charge + introduces free thiol. The new C685 sits in the dense 684-688 cluster — its thiol could engage in disulfide chemistry with other lumenal cysteines.

ΔΔG essentially neutral; AM 0.581 borderline + monogenic diabetes + DFNA6 confirm severe consequence.

Amino-acid chemistry
Arginine (R) → Cysteine (C) — long positively-charged guanidinium replaced by thiol.
Position in the protein
C-terminal lumenal domain · position 685 (pLDDT 90). Same as R685P.

Druggability Assessment

Category 4 — Stable Fold, Function Disrupted. ΔΔG ≈ 0. AlphaMissense 0.581 borderline + multi-phenotype confirm pathogenicity.

Mechanism: charge loss + free thiol introduction in dense 684-688 cluster. Therapeutic: same cluster target.

Why this matters

R685C is the FIFTH variant at position 685's microregion (R685P, R685C, A684T/V/G, Q687H). Densest multi-substitution hub in the Atlas.
Therapeutic Strategy Handoff · prediction

Feed this card to Wolfram Intelligence

Download the R685C PDF below and upload it to Wolfram Intelligence to generate therapeutic-strategy proposals — guanidinium mimetics, sigma-1 agonist docking, NAC thiol-capping. NAC is already on the bench-testing list.

Download R685C PDF card ↓Strategies are AI-generated predictions, not validated therapeutics.

UniProt Domain Annotation

Chain1890 · Wolframin
Topological domain653869 · Lumenal
Natural variant685685 · in DFNA6; dbSNP:rs142668478